THERAPEUTIC CLASS
A new medical therapy for anemia in thalassemia
In this issue of Blood, Piga et al report results of a phase 2, open label, nonrandomized, uncontrolled dose-finding study evaluating the effects of luspatercept on erythroid maturation and differentiation in adult patients with b-thalassemia.1 A high percentage of patients had an increase in hemoglobin or a reduction in transfusion burden, which helped lay the basis for
future randomized trials
No other version available